
{"id":124881,"date":"2025-03-24T10:45:23","date_gmt":"2025-03-24T09:45:23","guid":{"rendered":"https:\/\/ibecbarcelona.eu\/event\/workshop-2-net-rare-humanized-models-for-studying-rare-diseases\/"},"modified":"2025-06-11T15:47:50","modified_gmt":"2025-06-11T13:47:50","slug":"workshop-2-net-rare-humanized-models-for-studying-rare-diseases","status":"publish","type":"tribe_events","link":"https:\/\/ibecbarcelona.eu\/ca\/event\/workshop-2-net-rare-humanized-models-for-studying-rare-diseases\/","title":{"rendered":"Workshop 2. NET-RARE: Humanized Models for Studying Rare Diseases"},"content":{"rendered":"<p><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\"><strong>NET-RARE second workshop will explore<\/strong>\u00a0how\u00a0<strong>humanized and bioengineered models<\/strong>\u00a0can replace 2D cultures and murine models to\u00a0<strong>better understand<\/strong>\u00a0and replicate\u00a0<strong>rare disorders<\/strong>. The goal is to examine the latest approaches for studying rare diseases in personalized human models<strong>.<\/strong><\/span><\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">The opening seminar will feature\u00a0<strong>Juanma Fern\u00e1ndez\u00a0<\/strong><\/span>(IBEC)<span dir=\"ltr\" lang=\"EN-GB\">. He will present a 3D model designed to study various muscular diseases, along with Organ-on-Chip (OOC) technology and a biosensor platform for detecting biomarkers of the pathology. Next,\u00a0<strong>Anna Collado Gimbert\u00a0<\/strong><\/span>(<span dir=\"ltr\" lang=\"EN-GB\">VHIR<\/span>)\u00a0<span dir=\"ltr\" lang=\"EN-GB\">will introduce their new personalized model for studying rare anaemia disorders. Her team, in collaboration with IBEC, has developed a spleen-like microfluidic filtering unit to model disease progression and create a diagnostic device for prognosis and patient stratification.<\/span><\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">Following this,\u00a0<strong>international speaker Francesco Saverio Tedesco\u00a0<\/strong><\/span>(<span dir=\"ltr\" lang=\"EN-GB\">University College London<\/span>)\u00a0<span dir=\"ltr\" lang=\"EN-GB\">will present his research on enhancing muscle regeneration to develop treatments for severe and incurable childhood diseases, like muscular dystrophies. His team has developed a novel human engineered muscle model for advanced in vitro modelling of muscle disorders involving extracellular matrix, including COL6-related dystrophies.<\/span><\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">After a networking break, the next talk will be given by\u00a0<strong>Laura\u00a0<\/strong><\/span><\/span><span class=\"fontSizeLarge\"><span dir=\"ltr\" lang=\"EN-GB\"><strong>Siles<\/strong><\/span><\/span><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">\u00a0(<\/span><span class=\"fontColorNeutralPrimary\" dir=\"ltr\" lang=\"EN-GB\">Instituto de Microcirug\u00eda Ocular) in Barcelona<\/span><\/span><span class=\"fontSizeLarge\"><span class=\"fontColorNeutralPrimary\" dir=\"ltr\" lang=\"EN-GB\">.\u00a0<\/span><\/span><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">The group develops 3D retina models using induced pluripotent stem (iPS) cells and has extensive expertise in gene editing with CRISPR technology applied to patient-derived iPS cells. Finally,\u00a0<strong>Marc Riu-Villanueva<\/strong><\/span>(<span dir=\"ltr\" lang=\"EN-GB\">IBEC<\/span>)<span dir=\"ltr\" lang=\"EN-GB\">\u00a0will share their research on neurodegenerative diseases.<\/span><\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\"><strong>Join us to explore the next steps in bioengineering using humanized models to advance biomedical research!<\/strong><\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">Workshop held in the framework of the\u00a0<\/span><\/span><a href=\"https:\/\/ibecbarcelona.eu\/ca\/research\/ibec-intramural-thematic-networks\/\"><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">IBEC Thematic Networks<\/span><\/span><\/a><span class=\"fontSizeMediumPlus\"><span dir=\"ltr\" lang=\"EN-GB\">.<\/span><\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\"><i><span dir=\"ltr\" lang=\"EN-GB\">Registration (below) is mandatory.<\/span><\/i><\/span><\/p>\n<p>&nbsp;<\/p>\n<p><strong>Scheduled Program:\u00a0<\/strong><\/p>\n<p><span class=\"fontSizeMediumPlus\">09:20 \u2013 Registration<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">09:30 \u2013 Welcome and introduction<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">09:40 \u2013 Juanma Fern\u00e1ndez-Costa, IBEC Group \u201cBiosensors for Bioengineering\u201d, \u201c<i>Next-Gen preclinical models: Muscle-on-Chip meets nanoplasmonic biosensors for drug evaluation in muscular dystrophies<\/i>\u201d<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">10:10 \u2013 National invited speaker: Anna Collado Gimbert from the VHIR group \u201cChildhood Cancer and Blood disorders\u201d, \u201c<i>Deep characterization of red blood cells in sickle cell disease and other rare anemia disorders by microfluidics and machine learning algorithms<\/i>\u201d<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">10:40 \u2013 International invited speaker: Francesco Saverio Tedesco, professor of Neuromuscular Biology and Regenerative Medicine, Department of Cell and Developmental Biology, University College London (UK), \u201c<i>Advanced in vitro modelling of neuromuscular diseases and therapeutics<\/i>\u201d \u00a0<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">11:30 \u2013 Coffee break and Networking<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">12:00 \u2013 National invited speaker: Laura Siles from the Instituto de Microcirug\u00eda Ocular (IMO), \u201c<i>Retinal organoids and gene editing in Inherited Retinal Dystrophies: disease modeling using patient-derived iPSCs and potential therapeutic approximation<\/i>\u201d<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">12:30 \u2013 Marc Riu-Villanueva, IBEC group \u201cMolecular and Cellular Neurobiology\u201d, \u201c<i>Biochemistry and functional analysis of P301L Tau in human brain cortical organoids modelling tauopathies of the FTLD spectrum<\/i>\u201d<\/span><\/p>\n<p><span class=\"fontSizeMediumPlus\">13:00 \u2013 Remarks and Closing<\/span><\/p>\n<p>&nbsp;<\/p>\n<p>To register click <span style=\"color: #000000;\"><strong><a style=\"color: #000000;\" href=\"https:\/\/forms.office.com\/pages\/responsepage.aspx?id=13yxN8VLc0y4uiWDJ_cI73xju0M0r8VIpvgkraQBC8tUOUtYQlY0RzExME9ITDJZRURSNVBSUzVQVC4u&amp;route=shorturl\">here<\/a><\/strong><\/span><\/p>\n","protected":false},"excerpt":{"rendered":"<p>NET-RARE second workshop will explore\u00a0how\u00a0humanized and bioengineered models\u00a0can replace 2D cultures and murine models to\u00a0better understand\u00a0and replicate\u00a0rare disorders. The goal is to examine the latest approaches for studying rare diseases &#8230; <a title=\"Workshop 2. NET-RARE: Humanized Models for Studying Rare Diseases\" class=\"read-more\" href=\"https:\/\/ibecbarcelona.eu\/ca\/event\/workshop-2-net-rare-humanized-models-for-studying-rare-diseases\/\" aria-label=\"More on Workshop 2. NET-RARE: Humanized Models for Studying Rare Diseases\">Read more<\/a><\/p>\n","protected":false},"author":54,"featured_media":0,"template":"","meta":{"_tribe_events_status":"","_tribe_events_status_reason":"","footnotes":""},"tags":[],"tribe_events_cat":[358],"class_list":["post-124881","tribe_events","type-tribe_events","status-publish","hentry","tribe_events_cat-symposium-ca","cat_symposium-ca"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.4 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Workshop 2. NET-RARE: Humanized Models for Studying Rare Diseases - Institute for Bioengineering of Catalonia<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/ibecbarcelona.eu\/ca\/event\/workshop-2-net-rare-humanized-models-for-studying-rare-diseases\/\" \/>\n<meta property=\"og:locale\" content=\"ca_ES\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Workshop 2. NET-RARE: Humanized Models for Studying Rare Diseases - Institute for Bioengineering of Catalonia\" \/>\n<meta property=\"og:description\" content=\"NET-RARE second workshop will explore\u00a0how\u00a0humanized and bioengineered models\u00a0can replace 2D cultures and murine models to\u00a0better understand\u00a0and replicate\u00a0rare disorders. The goal is to examine the latest approaches for studying rare diseases ... 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